“Simply put, we believe the gene therapy demonstrated in both animal species ... designed a dual-function recombinant adeno-associated virus serotype 9 vector to deliver a gene replacement ...

ReGenX's AAV Vector Technology gives extremely efficient and stable gene expression in neonatal and adult animals, and can be used to create disease models and to study gene function and target ...

which is the naturally occurring AAV serotype that is currently understood to have the best penetration of the BBB in humans. “We believe Voyager’s TRACER capsids should allow significantly ...

Each AAV serotype exhibits unique properties that influence tissue tropism and therapeutic goal, allowing tailored approaches for gene therapy applications. With the absolute quantification provided ...