Gene editing with adeno-associated virus vector offers hope for hereditary deafness
An R75W mutation in the gap junction β2 (GJB2) gene causes severe fragmentation of gap junction plaques, connecting adjacent ...
EurekAlert!3d
New study reveals the curative potential of genome editing approach for genetic deafness
R75W mutation in the gap junction β2 (GJB2) gene causes severe fragmentation of gap junction plaques, connecting adjacent ...
PharmaTimes3d
Genome editing offers hope for genetic hearing loss
Scientists from Juntendo University and The University of Tokyo have created an adeno-associated virus (AAV)-based genome ...
GEN - Genetic Engineering and Biotechnology News12d
DMD Patient Dies After Treatment with Sarepta Gene Therapy
The patient, whom Sarepta described as a young man and later told news outlets was 16 years old, suffered acute liver failure ...
OXB honoured at 2025 CDMO Leadership Awards in 'Cell & Gene Therapy – Global' category
OXB honoured at 2025 CDMO Leadership Awards in 'Cell & Gene Therapy – Global' category Oxford, UK – 21 March 2025: OXB (LSE: ...
Labroots10d
BalanCD HEK293 Viral Feed: Accelerating AAV and LV Production for Gene and Cell Therapy
Efficient viral vector production is essential for the cost-effective ... that addition of the feed medium 24 hours post-transfection increased adeno-associated virus (AAV) titer by 3-fold to 10-fold ...
Contract Pharma13d
ChromaTan and Landmark Bio Receive NIIMBL Grant
Funds will help the companies create a platform for the manufacturing and characterization of AAV-based gene therapy vectors.