Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...
Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.
In 2019, the first CRISPR clinical trials were conducted to treat sickle cell diseases and in 2020, this treatment was ...
A GROUNDBREAKING genetic treatment with the potential to cure sickle cell disease will be rolled out on the NHS. The one-off ...
People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...
A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...
Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease (SCD), Casgevy, has been given the ...
Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...
A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle cell disease. Casgevy, also ...
One sickle cell patient told ITV News the new gene therapy being rolled out for use on the NHS means they "finally have something to look towards". | ITV National News ...
Around 1,700 people could be eligible for the one-time treatment, which is seen as a less risky alternative to a donor stem ...