A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new study ...

News broke yesterday that researchers in Philadelphia appear to have successfully treated a 6-month-old baby boy, called KJ, with a personalized CRISPR gene-editing therapy. The treatment corrects ...

The rare genetic disease kills 50% of babies diagnosed with it by early infancy. Just six months after a newborn at Children's Hospital of Philadelphia was diagnosed with a rare and life ...

Featured Host, "CBS Mornings;" Anchor, "CBS News 24/7" Vladimir Duthiers is a featured host of "CBS Mornings" and serves as anchor for CBS News 24/7. The Peabody Award- and Emmy Award-winning ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. FDA OKs first blood test that can help ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. A boy likely died from drinking too much olive ...

You can reach Jason on Signal at JasonMast.05. NEW ORLEANS — Greetings from ASGCT, where the gene therapy field had some great news for once, about a highly photogenic infant. Kiran Musunuru ...

Gene therapies, which can be extremely expensive to develop, generally target more common disorders in part for simple financial reasons: more patients mean potentially more sales, which can help ...

Gene Editing Helped a Desperately Ill Baby Thrive. Scientists Say It Could Someday Treat Millions A baby born with a rare and dangerous genetic disease is growing and thriving after getting an ...

May 13, 2025 — Researchers developed a new machine learning method that, given a relevant amino acid sequence, can automatically predict the location of a protein ... Genome of Near-Extinct ...