gene therapy, Blind Children and Moorfields Eye Hospital

Blind Children See After 'Remarkable' Rare Eye Disorder Breakthrough
Researchers from London's Moorfields Eye Hospital, biotech firm MeiraGTx and University College London have demonstrated that their therapy is both safe and effective in improving the vision of and slowing retinal deterioration in young patients born with "LCA-AIPL1."
MeiraGTx gene therapy allows 11 blind children to see as biotech eyes accelerated approval
Eleven children who were legally blind at birth all gained visual acuity after receiving MeiraGTx's investigational gene therapy, data that is prompting the biotech to seek accelerated approval in AIPL1-associated severe retinal dystrophy.
Blind Children See for the First Time Thanks to a Revolutionary Gene Therapy
A groundbreaking gene therapy has restored sight in four young children born with severe blindness due to a rare genetic deficiency. Scientists at UCL and Moorfields Eye Hospital successfully injected healthy copies of the defective gene into the retina,
Blind Boy Can See After Groundbreaking Gene Therapy
A young boy, by the name of Harvey, is seen before and after he received gene supplement therapy for a rare inherited eye disorder that caused him to be blind. The after results show a miraculous development in his eyesight.
Medics preserve sight in children with rare genetic eye condition in world first
Medics in the UK have become the first in the world to successfully administer a pioneering gene therapy that preserves sight in young children with an extremely rare genetic condition that usually causes blindness in the first few years of life.
Gene therapy experiment gives children 'life-changing' sight boost
An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood ...
Nature4y
Environmental Influences on Gene Expression
For example, Himalayan rabbits carry the C gene, which is required for the development of pigments in the fur, skin, and eyes ... This temperature regulation of gene expression produces ...
Medindia6y
Study Finds Eye Cancer Gene’s Role in Retinal Development
“On the basis of our data, we propose that N-myc plays a central role in coordinating retinal proliferation with eye growth during development.” Genes in the Myc family carry out vital roles ...
Nanowerk9mon
Gene Regulation: The Master Control of Cellular Function
Gene regulation is the process by which cells control the expression of their genes, determining when, where, and to what extent each gene is expressed. It is a fundamental mechanism that ...