A Connecticut boy is among four children all born with severe childhood blindness who gained “life-changing improvements” to ...

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood ...

Bluebird Bio will sell itself to private equity firms Carlyle and SK Capital for about $30 million, the company said Friday.

Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...

One of the largest pharmaceutical companies in North Carolina is discontinuing a treatment produced in the state.

A groundbreaking gene therapy has restored sight in four young children born with severe blindness due to a rare genetic ...

Gene therapy represents a paradigm shift in modern medicine, offering unprecedented opportunities to combat diseases at their ...

Gene therapy stocks are transforming healthcare with revolutionary treatments. Therefore, as this sector continues to evolve, ...

Pfizer is pulling further away from the gene therapy field with its decision to discontinue hemophilia product Beqvez. | ...

A new inhalable gene therapy for cystic fibrosis (CF) has entered Phase I clinical trials, a major milestone on the journey ...