News

Smithsonian Magazine8h
In a Remarkable First, a Baby With a Rare Disease Receives Personalized Gene Therapy
Researchers say the CRISPR-based technique used could eventually be employed to treat more people with rare genetic diseases ...
Nature6d
World’s first personalized CRISPR therapy given to baby with genetic disease
Treatment seems to have been effective, but it is not clear whether such bespoke therapies can be widely applied.
First-Ever Custom CRISPR Therapy Saves Infant With Deadly Genetic Disorder
A pivotal medical milestone has been reached. For the first time ever, researchers have used a personalized CRISPR-based gene ...
Gene editing saves Pennsylvania baby with rare genetic disease
He’s among the first to be successfully treated with a custom therapy that seeks to fix a tiny but critical error in his ...
Doctors Achieve Medical Breakthrough Using Gene-Editing Therapy to Heal Baby with Rare Disorder
Doctors have successfully used gene-editing therapy to treat an infant born with a rare disorder. Experts believe the ...
Child treated with gene editing therapy for the first time by a team of Philadelphia doctors
A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology ...
Personalized CRISPR treatment used on baby with genetic disease
KJ received the bespoke CRISPR treatment 6.5 months after birth, receiving three infusions of the therapy as of April 2025.
A Gene-Editing Breakthrough Saves Infant With Rare Disease
The Crispr therapy was tailored to the baby’s specific condition and could provide a template for others.
Doctors successfully treated a baby with the first ever personalized gene-editing therapy
A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...
New Scientist on MSN5d
Baby with rare disease given world-first personal CRISPR gene therapy
By Michael Le PageA baby boy with a life-threatening genetic condition has become the first person to receive a bespoke ...
Managed Healthcare Executive1d
Breakthrough Gene Therapy Saves Infant with Rare Metabolic Disease
A personalized gene editing therapy was successfully used to treat an infant with CPS1 deficiency, a disease that causes ...
Science Daily5d
Infant with rare, incurable disease is first to successfully receive personalized gene therapy treatment
A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was diagnosed with the ...