Columnist Jennifer Lynne stresses the significance of hidden symptoms in the lives of those with bleeding disorders.

Approved in 2022 by the FDA, Hemgenix is the first gene therapy for the treatment of adults with hemophilia B who currently use factor IX prophylaxis therapy, have current or historical life ...

But in January, everything changed. “He just wakes up and his whole body is swollen to where he is just not the same child,” Matthew Lambert said. Alarmed, Kamden’s parents took him to a doctor.