A nonprofit called the n-Lorem Foundation is working on developing an individualized treatment that targets the genetic cause of rare diseases.

For Uditi’s parents, reading about use of CRISPR tech, or ‘genetic scissors’, to treat baby KJ, diagnosed with severe genetic ...

Donations made Monday at Dartmouth College can go a long way toward helping people with the most common genetic blood disorder in the United States.

For the first time in New Hampshire, the American Red Cross hosted a blood drive meant to help people with sickle cell disease.

An infant in Pennsylvania became the first patient treated with personalized CRISPR for a fatal genetic disorder, showing ...

Doctors announced this week that they have treated a newborn baby with a rare genetic disease using the world’s first personalized gene editing therapy. Geoff Bennett discussed the treatment and its ...

A mother has chosen to return to her home country with her 11-year-old daughter, who has a rare genetic disorder, after being ...

Baby born with rare life-threatening disorder makes medical history - Researchers hope what they learn from KJ will help ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.

A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology ...

Fargo’s Aldevron helped create a custom gene-editing therapy that cured a baby of urea cycle disorder, a rare and potentially ...

Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can ...